BBC News: Gene therapy for rare eye disease set to be offered on NHS

4 September 2019
Source: BBC News

Patients with a rare inherited eye disorder are set to be able to access a new gene therapy on the NHS which slows down sight loss. Draft NICE guidance recommends the therapy (Luxturna) to treat inherited retinal dystrophies. The National Institute for Health and Care Excellence estimates just under 90 people in England will be eligible for the treatment. Drug

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Retina UK: Gene therapy for RPE65 gene approved for use in EU

23 November 2018
Source: Retina UK

The gene therapy Luxturna has won European regulatory approval for the treatment of Inherited retinal dystrophy caused by mutations in the RPE65 gene. This milestone decision was made by the European Medicines Agency (EMA) on Thursday, 22 November. Luxturna is the first and only gene therapy available in Europe to treat inherited retinal disease. It had already been approved for

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